NPR

FDA Approves First Drug For A Rapid Aging Disorder In Children

A newly approved drug can extend the lives of children with progeria, a rare disorder that causes rapid aging. The drug is the result of one family's effort to help a child with the fatal condition.
Sam Berns and Audrey Gordon, executive director of The Progeria Research Foundation and Berns's aunt, attend The New York Premiere Of HBO's "Life According To Sam" on October 8, 2013 in New York City.

The Food and Drug Administration has approved a drug that extends the lives of children with an extremely rare genetic disorder that causes them to grow old before they grow up.

The disorder, , ages cells rapidly and prematurely. As a result, affected children remain small and begin to look frail and old by the time they reach school age. Most die of heart disease in

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