41 min listen
Novel Therapies: Entering Uncharted Territory
Novel Therapies: Entering Uncharted Territory
ratings:
Length:
63 minutes
Released:
Mar 17, 2022
Format:
Podcast episode
Description
Gene therapy, hemostatic rebalancing therapies, memetic therapies, and even factor replacement therapy are all currently being explored in clinical trials, but while these therapies are paving the way to historical treatment ease and efficacy, they are also sweeping the hemophilia community into uncharted territory of potentially new challenges that must be addressed. This episode explores the current state of novel therapy investigation in hemophilia. Contributors: Dr. Maria Elisa Mancuso Dr. Glenn Pierce Dr. Steven Pipe Dr. Lindsey George Dr. Margareth Ozelo Dr. Guy Young Dr. Michael Recht Dr. Rich Gorman Mark Skinner Luke Pembroke Senior Advisor: Dr. Donna DiMichele Links to learn more: Future Therapies - National Hemophilia Foundation 2021 clinical trials update: Innovations in hemophilia therapy Advances in the management of haemophilia: emerging treatments and their mechanisms Emerging drugs for hemophilia A: insights into phase II and III clinical trials Discussing investigational AAV gene therapy with hemophilia patients: A guide Hemophilia Clinical Trials - ClinicalTrials.gov Show Notes: Featured Advertiser: Sanofi Subscribe to BloodStream Media’s Global Hemophilia Report Connect with the Global Hemophilia Report Global Hemophilia Report on LinkedIn Global Hemophilia Report on Twitter Global Hemophilia Report on Facebook Connect with BloodStream Media: BloodStreamMedia.com BloodStream on Facebook BloodStream on Twitter
Released:
Mar 17, 2022
Format:
Podcast episode
Titles in the series (29)
Inhibitors: Prevention, Eradication, and Lived Experiences: Inhibitor development has long been considered the most significant complication of severe hemophilia, but with the licensure of the first non-factor therapy and a robust pipeline of novel and gene therapeutics being investigated, is it still of... by Global Hemophilia Report