15 min listen
Developing Novel Treatments for Rare Disorders: A Look at MPS I with Dr. Emil Kakkis
FromWCG Talks Trials
Developing Novel Treatments for Rare Disorders: A Look at MPS I with Dr. Emil Kakkis
FromWCG Talks Trials
ratings:
Length:
19 minutes
Released:
Jan 13, 2020
Format:
Podcast episode
Description
In this episode, WCG’s President of Patient Advocacy, Steve Smith, talks with Emil Kakkis, MD, PhD, Chief Executive Officer of Ultragenyx Pharmaceuticals and President of the non-profit EveryLife Foundation for Rare Diseases organization. Known for his work in developing an enzyme replacement therapy for the rare disorder MPS I and his connection to the Ryan Foundation, Dr. Kakkis shares with us his experiences in being involved in bringing drugs to market and forming relationships with patients along the way.
Released:
Jan 13, 2020
Format:
Podcast episode
Titles in the series (67)
Important Trends in CNS Clinical Trials with guest Cristoph Correll, MD by WCG Talks Trials