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STAT+: Muscular dystrophy patient who was first in line for a custom CRISPR therapy dies

A man with muscular dystrophy who was first in line to receive an experimental CRISPR therapy tailor made to treat the cause of his rare form of the disease has…
Terry Horgan was part of a trial of an experimental gene-editing therapy for muscular dystrophy.

A man with muscular dystrophy who was first in line to receive an experimental gene editing therapy tailor made to treat the cause of his rare form of the disease has died.

The creation of  for Terry Horgan, 27, was helmed by the Boston and Connecticut based nonprofit Cure Rare Disease — founded and led by Terry’s older brother, Richard Horgan. Terry was slated to finally receive the therapy

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