Discover this podcast and so much more

Podcasts are free to enjoy without a subscription. We also offer ebooks, audiobooks, and so much more for just $11.99/month.

Major FDA approvals for Vertex/CRISPR; bluebird gets black box warning and price scrutiny

Major FDA approvals for Vertex/CRISPR; bluebird gets black box warning and price scrutiny

FromBioSpace


Major FDA approvals for Vertex/CRISPR; bluebird gets black box warning and price scrutiny

FromBioSpace

ratings:
Length:
17 minutes
Released:
Dec 13, 2023
Format:
Podcast episode

Description

That was Week with a capital W. Two major FDA approvals for sickle cell came through on Friday - Casgevy, the first-ever CRISPR-based gene editing therapy from Vertex and CRISPR Therapeutics, and bluebird bio’s Lyfgenia, which comes with a hefty price tag and a black box warning. 
Axcella announced its closure; what does the future of long-covid treatments look like, especially as attention shifts to different markets like ADCs and neurological treatments? 
Also discussed - Vanda drops $100m on rights to MS drug Ponvory, AI regulatory developments in Europe. 
BioSpace's Lori Ellis, Greg Slabodkin and Tyler Patchen discuss.
Released:
Dec 13, 2023
Format:
Podcast episode

Titles in the series (46)

Unravel the business of science with BioSpace. We dive into biopharma's top stories and biggest challenges, whether it’s layoffs, pipeline shake-ups, acquisitions, new FDA approvals or how to regulate AI in drug development.