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Oligonucleotide Opportunities in DMD with PepGen's James McArthur, Ph.D.

Oligonucleotide Opportunities in DMD with PepGen's James McArthur, Ph.D.

FromBusiness Of Biotech


Oligonucleotide Opportunities in DMD with PepGen's James McArthur, Ph.D.

FromBusiness Of Biotech

ratings:
Length:
36 minutes
Released:
Jul 25, 2022
Format:
Podcast episode

Description

Among the more prevalent genetic conditions, Duchenne muscular dystrophy  affects an estimated one in 3,500 male births worldwide.  It's caused by mutations of the DMD gene, which  regulates the production of a protein called dystrophin. Approved DMD treatments haven't demonstrated strong clinical outcomes, but James McArthur, Ph.D. and his team at PepGen are seeking to change that with a pipeline of disease-modifying peptide-conjugated oligonucleotide candidates derived from the company's Enhanced Delivery Oligonucleotide platform. The Business of Biotech caught up with Dr. McArthur at PepGen's Cambridge headquarters to learn more. Catch up on more gene therapy development advances on bioprocessonline.com.
Released:
Jul 25, 2022
Format:
Podcast episode

Titles in the series (100)

The Business of Biotech is the pod dedicated to leaders of emerging biopharma firms. We bring you insight into organizational, finance and funding, HR, clinical, manufacturing, and regulatory challenges you’ll face as you navigate your company from an idea to success in the clinic. Each episode features guest commentary and best practices from accomplished founders and biopharma industry luminaries. The Business of Biotech is produced by BioProcess Online and brought to you by Cytiva, formerly GE Healthcare Life Sciences.