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Oligonucleotide Opportunities in DMD with PepGen's James McArthur, Ph.D.
Oligonucleotide Opportunities in DMD with PepGen's James McArthur, Ph.D.
ratings:
Length:
36 minutes
Released:
Jul 25, 2022
Format:
Podcast episode
Description
Among the more prevalent genetic conditions, Duchenne muscular dystrophy affects an estimated one in 3,500 male births worldwide. It's caused by mutations of the DMD gene, which regulates the production of a protein called dystrophin. Approved DMD treatments haven't demonstrated strong clinical outcomes, but James McArthur, Ph.D. and his team at PepGen are seeking to change that with a pipeline of disease-modifying peptide-conjugated oligonucleotide candidates derived from the company's Enhanced Delivery Oligonucleotide platform. The Business of Biotech caught up with Dr. McArthur at PepGen's Cambridge headquarters to learn more. Catch up on more gene therapy development advances on bioprocessonline.com.
Released:
Jul 25, 2022
Format:
Podcast episode
Titles in the series (100)
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