Enzyme therapy approved for rare genetic condition in babies
by Storm Newton
Nov 27, 2023
2 minutes
A treatment for a rare genetic condition that usually kills babies before they turn one is to be made available in England in a first for the NHS.
It is hoped the move will help save the lives of babies and toddlers born with Wolman disease, a type of lysosomal acid lipase deficiency that occurs in one in
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